Search for Clinical Trial Results

Mucopolysaccharidosis Type III - 54 Studies Found
Status | Study |
Active, not recruiting |
Study Name: Extension of Study HGT-SAN-055 Evaluating Administration of rhHNS in Patients With Sanfilippo Syndrome Type A (MPS IIIA) Condition: Sanfilippo Syndrome Date: 2011-02-16 Interventions:
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Completed |
Study Name: A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA) Condition: Sanfilippo Syndrome Type A Date: 2010-01-11 Interventions: Other: assessment Physical, developmental, neurological, behavioral, and neurocognitive assessments |
Active, not recruiting |
Study Name: Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy Condition:
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Completed |
Study Name: Intracerebral Gene Therapy for Sanfilippo Type A Syndrome Condition:
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Completed |
Study Name: Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) Condition: Sanfilippo Syndrome Type B Date: 2012-01-10 |
Completed |
Study Name: Neurobehavioral Phenotypes in MPS III Condition:
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Recruiting |
Study Name: A Treatment Study of Mucopolysaccharidosis Type IIIB Condition:
Date: 2016-02-27 Interventions: Drug: BMN 250 Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human ins |
Completed |
Study Name: Safety, Tolerability, Ascending Dose and Dose Frequency Study of rhHNS Via an IDDD in MPS IIIA Patients Condition: Sanfilippo Syndrome Type A (MPS IIIA) Date: 2010-06-24 Interventions:
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Recruiting |
Study Name: Biomarker for Sanfilippo Disease Condition:
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Completed |
Study Name: Randomized, Controlled, Open-label, Multicenter, Safety and Efficacy Study of rhHNS Administration Via an IDDD in Pediatric Patients With Early Stage MPS IIIA Disease Condition: Sanfilippo Syndrome Date: 2014-02-10 Interventions: Drug: Recombinant human heparan N-sulfatase [rhHNS] Recombinant human heparan N-sulfatase [rhHNS] |