Search for Clinical Trial Results

Congenital Erythropoietic Porphyria - 25 Studies Found
Status | Study |
Recruiting |
Study Name: Controlled Trial of Panhematin in Treatment of Acute Attacks of Porphyria Condition: Acute Porphyrias Date: 2014-06-25 Interventions:
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Completed |
Study Name: Observational Study of Acute Intermittent Porphyria Patients Condition: Acute Intermittent Porphyria Date: 2014-02-27 |
Recruiting |
Study Name: Longitudinal Study of the Porphyrias Condition:
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Recruiting |
Study Name: A Phase 1 Study of ALN-AS1 in Patients With Acute Intermittent Porphyria (AIP) Condition: Acute Intermittent Porphyria Date: 2015-05-19 Interventions:
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Recruiting |
Study Name: Hydroxychloroquine and Phlebotomy for Treating Porphyria Cutanea Tarda Condition: Porphyria Cutanea Tarda Date: 2012-04-05 Interventions:
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Completed |
Study Name: Phase I Gene Therapy Clinical Trial Using the Vector rAAV2/5-PBGD for the Treatment of Acute Intermittent Porphyria Condition: Acute Intermittent Porphyria Date: 2014-02-28 Interventions:
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Enrolling by invitation |
Study Name: A Study to Evaluate Long-term Safety and Clinical Activity of ALN-AS1 in Patient With Acute Intermittent Porphyria (AIP) Condition: Acute Intermittent Porphyria Date: 2016-10-28 Interventions: Drug: ALN-AS1 ALN-AS1 by subcutaneous (SC) injection |
Completed |
Study Name: Risk Factors of Porphyria Cutanea Tarda (PCT) Condition: Porphyria Cutanea Tarda Date: 2005-09-13 |
Completed |
Study Name: Pilot Trial of Deferasirox in the Treatment of Porphyria Cutanea Tarda Condition: Porphyria Cutanea Tarda Date: 2008-01-10 Interventions: Drug: Deferasirox 250 mg of deferasirox once daily for 6 months |
Not yet recruiting |
Study Name: Dental Health, Diet, Inflammation and Biomarkers in Patients With Acute Intermittent Porphyria(AIP) Condition: Acute Intermittent Porphyria Date: 2012-06-05 |